Mucopolysaccharidosis Treatment companies

  • Report ID: 5215
  • Published Date: Sep 26, 2025
  • Report Format: PDF, PPT

Key Mucopolysaccharidosis (MPS) Treatment Market Players:

    The international mucopolysaccharidosis (MPS) treatment market is an oligopoly, which is readily dominated by innovative biotechs and specialized pharmaceutical giants. Besides, notable strategic initiatives include relentless research and development (R&D) funding in cutting-edge therapies, including CNS-penetrant ERTs and gene therapy, with the intention to cater to increased demand for neurological symptoms. Meanwhile, organizations are strongly pursuing orphan drug designations for premium pricing and market exclusivity; for instance, Takeda and BioMarin have leveraged their respective established commercial facilities for worldwide launches, thereby proliferating the mucopolysaccharidosis (MPS) treatment market globally.

    Here is a list of key players operating in the global market:

    • BioMarin Pharmaceutical Inc. (U.S.)
      • Company Overview
      • Business Strategy
      • Key Product Offerings
      • Financial Performance
      • Key Performance Indicators
      • Risk Analysis
      • Recent Development
      • Regional Presence
      • SWOT Analysis
    • Sanofi (France)
    • Regenxbio Inc. (U.S.)
    • UCB S.A. (Belgium)
    • Inventiva Pharma (France)
    • ArmaGen, Inc. (U.S.)
    • Denali Therapeutics Inc. (U.S.)
    • Sangamo Therapeutics, Inc. (U.S.)
    • Abeona Therapeutics Inc. (U.S.)
    • Green Cross Corp. (South Korea)
    • GC Pharma (South Korea)
    • Amicus Therapeutics, Inc. (U.S.)
    • M6P Therapeutics (U.S.)
    • Passage Bio, Inc. (U.S.)
    • Sarepta Therapeutics, Inc. (U.S.)

Browse key industry insights with market data tables & charts from the report:

Frequently Asked Questions (FAQ)

In the year 2025, the industry size of the mucopolysaccharidosis (MPS) treatment market was over USD 4.4 billion.

The market size for the mucopolysaccharidosis (MPS) treatment market is projected to reach USD 11 billion by the end of 2035 expanding at a CAGR of 10.8% during the forecast period i.e., between 2026-2035.

The major players in the market are BioMarin Pharmaceutical Inc., Sanofi Regenxbio Inc., UCB S.A., Inventiva Pharma, and others.

In terms of the route of administration segment, the intravenous segment is anticipated to garner the largest market share of 77.3% by 2035 and display lucrative growth opportunities during 2026-2035.

The market in North America is projected to hold the largest market share of 45.2% by the end of 2035 and provide more business opportunities in the future.
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