Spinal Muscular Atrophy Treatment Market Analysis

  • Report ID: 2724
  • Published Date: Sep 08, 2025
  • Report Format: PDF, PPT

Spinal Muscular Atrophy Treatment Market Segmentation:

Treatment Type Segment Analysis

The medication segment is expected to register a considerable share in the spinal muscular atrophy treatment market. The segment is driven by the widespread use of RNA-based drugs such as Biogen’s Spinraza. Additionally, newer medicines including Evrysdi have provided more convenient and accessible options for patients, further bolstering the medication segment. These drugs are favored as they offer ongoing treatment options compared to one-time, high-cost gene therapies. Moreover, both oral and injectable formulations’ availability, improved accessibility to treatment, permitting different preferences and needs to be met with effective therapy. The continuous need for dosage over time provides a steady demand, making medications a key revenue-generating segment in the market.

Route of Administration Segment Analysis

Oral segment is likely to dominate spinal muscular atrophy treatment market share of over 62.9% by 2035. Administration of oral SMA treatments at home does not require clinical visits, reducing the load on patients and their families. It is particularly convenient for long-term treatment regimens, as visits to hospitals can be disruptive. This thereby drives the market growth significantly. Furthermore, oral therapies eliminate the need for healthcare resources including nursing support for injections or infusion centers. Cost savings due to this make oral treatments a more appealing option for payers and providers, hence, accelerating their adoption and boosting market growth.

Our in-depth analysis of the market includes the following segments:

Treatment Type

  • Medication
    • Gene therapy
    • Antisense oligonucleotides
    • Other medications
  • Supportive care
    • Physical therapy
    • Respiratory support
    • Nutritional support
  • Spinal surgery

Type

  • Werdnig-Hoffmann disease
  • Infant SMA
  • Kugelberg-Welander disease
  • Adult SMA

Route of Administration

  • Oral
  • Parenteral

End use

  • Hospitals
  • Specialty clinics
  • Homecare settings
  • Other end-users

Browse key industry insights with market data tables & charts from the report:

Frequently Asked Questions (FAQ)

In the year 2026, the industry size of spinal muscular atrophy treatment is estimated at USD 5.94 billion.

The global spinal muscular atrophy treatment market size crossed USD 5.13 billion in 2025 and is likely to register a CAGR of over 17.5%, exceeding USD 25.73 billion revenue by 2035.

North America spinal muscular atrophy treatment market will dominate over 48.90% share by 2035, driven by the presence of leading biotechnology firms at the forefront of developing novel therapies, a robust healthcare infrastructure, and strong government support in North America.

Key players in the market include PTC Therapeutics, Voyager Therapeutics, Inc, Astellas Pharma Inc., Novartis AG, Pfizer, Inc., F. Hoffmann-La Roche Ltd, CYTOKINETICS, INC., Ionis Pharmaceuticals, Inc., Regeneron Pharmaceuticals, Inc.
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